Tag Archives: genetic disorder

Lindsey Johnson Edwards: Navigating Life and Empowering Others with CLOVES Syndrome

Lindsey Johnson Edwards uses TikTok to share her journey with CLOVES syndrome, a rare vascular.....Read more

FDA Grants Rare Pediatric Disease Designation to NS-050/NCNP-03 for Duchenne Muscular Dystrophy

FDA grants Rare Pediatric Disease Designation to NS-050/NCNP-03 for Duchenne muscular dystrophy (DMD). This promising.....Read more