Tag Archives: genetic disorder
How I Met Your Mother Cast Reunites for Charity Concert Benefiting Rare Disorder Research
The How I Met Your Mother cast reunited for a charity concert benefiting Jacobsen syndrome.....Read more
13
Jan
Jan
Lindsey Johnson Edwards: Navigating Life and Empowering Others with CLOVES Syndrome
Lindsey Johnson Edwards uses TikTok to share her journey with CLOVES syndrome, a rare vascular.....Read more
13
Dec
Dec
FDA Grants Rare Pediatric Disease Designation to NS-050/NCNP-03 for Duchenne Muscular Dystrophy
FDA grants Rare Pediatric Disease Designation to NS-050/NCNP-03 for Duchenne muscular dystrophy (DMD). This promising.....Read more
05
Dec
Dec